Go to content

In The News

From One Patient to Many: How Baby KJ is Ushering in a New Era in CRISPR Medicine

Read about From One Patient to Many: How Baby KJ is Ushering in a New Era in CRISPR Medicine

Baby KJ’s doctors will ask FDA this winter to OK a clinical trial of pioneering gene editing approach

Squirming toddler with a rare liver disease leaves barely a dry eye at STAT Summit

Read about Baby KJ’s doctors will ask FDA this winter to OK a clinical trial of pioneering gene editing approach

Advancing gene editing: the role of lipid nanoparticles in CRISPR delivery

CRISPR therapies depend on delivery and lipid nanoparticles are emerging as a more flexible and scalable option than viral vectors.

Read about Advancing gene editing: the role of lipid nanoparticles in CRISPR delivery

Baby Steps: Kiran Musunuru Lays Out the Path Beyond KJ at ESGCT

Read about Baby Steps: Kiran Musunuru Lays Out the Path Beyond KJ at ESGCT